Daybue, Daybue Stix

What is this medication? Daybue, which contains the active ingredient trofinetide, is a prescription medication used to treat Rett syndrome in adults and children aged two years and older. Rett syndrome is a rare genetic neurological disorder that leads to severe impairments in a person's ability to speak, walk, eat, and breathe. This medication is significant because it is the first drug approved by the Food and Drug Administration specifically designed to address the symptoms of this complex developmental condition.

The medication is available as an oral solution and is typically administered twice daily, either by mouth or through a gastrostomy tube. It works by potentially reducing inflammation in the brain and supporting the function of synapses, which are the points of communication between nerve cells. While Daybue does not cure Rett syndrome, it is intended to improve daily functioning and behavior, providing a therapeutic option for patients and families managing the lifelong challenges of the disorder.